Designer babies may sound like science fiction, but they’re becoming increasingly possible as gene editing technology to treat and prevent genetic diseases evolves. How scientists should use it ...

We focus on the mouse as a model organism or the development of new technologies and preclinical testing of gene editing therapies. The center leverages the expertise of its members in the evaluation ...

The mutation in the huntingtin (HTT) gene, which causes the incurable ... They found that mutated HTT undergoes a process called “somatic expansion,” by which the number of CAG repeats ...