In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and bone marrow transplantation—to alleviate symptoms of multiple sulfatase ...

“Cell and gene therapy manufacturing, supply chains and delivery are all very complex,” Anita Ralli, chair of the Collective and associate director of government affairs at Gilead ...

In a significant step forward for India’s cancer treatment, Immuneel Therapeutics, a leading cell and gene therapy statrtup backed by entrepreneur Kiran Mazumdar-Shaw, has unveiled Qartemi, the ...

Gene therapy, on the other hand, offers a promising alternative, using cells from the patient that have been corrected ex vivo. However, due to the complexity of cells with a compromised DNA repair ...

Although these diseases were initially treated by transplantation of allogeneic hematopoietic stem cells, the past 20 years has shown that these conditions are correctable by gene therapy.

Take a look overseas, the U.S. market currently counts 43. However, since 2020, the European Medical Agency (EMA) has made notable progress in approving advanced therapy medicinal products (ATMPs) – ...