Ultragenyx Pharmaceutical RARE reported new findings from an ongoing, pivotal study of its investigational candidate, UX111 (ABO-102) AAV gene therapy, for Sanfilippo syndrome type A (MPS IIIA). Per ...

South San Francisco, CA, January 30, 2025 – The California Institute for Regenerative Medicine (CIRM), one of the world’s largest institutions dedicated to regenerative medicine, has awarded nearly ...

Chinese scientists achieve genetic breakthrough by breeding baby mice using DNA from two male parents, opening new ...

If successful OPT-302 would be the first superior treatment in more than 15 years for wet-AMD, which affects around 3.5 ...

Cushing's syndrome is a hormonal disorder. It’s caused when you have high levels of the hormone cortisol over a long time. Cushing's syndrome is fairly rare. It most often affects adults who are 20 to ...

Angelman Syndrome is a rare genetic disorder caused by UBE3A gene mutations, leading to developmental delays, speech issues, seizures, and distinct behaviors like frequent laughter and hyperactivity.

For most adults a 100-piece puzzle will likely be too easy, but a 1000-piece puzzle might cause you to get frustrated and lose interest. Because of this, you need to consider how much time you're ...

Dawes added: "Today, this starts to change." "As age checks start to roll out in the coming months, adults will start to notice a difference in how they access certain online services. Services which ...

SINGAPORE - From March 31, app stores must block young users below 18 years old from downloading apps not meant for their age group, including dating app Tinder and adult video games like Grand ...

Javascript must be enabled to use this site. Please enable Javascript in your browser and try again. Apply now for the AARP Purpose Prize award, which honors people ...